Search Results

University of Cagliari Researcher Furthers Understanding of Gene Therapy (Beta Thalassemia in Children: Established Approaches, Old Issues, New Non-Curative Therapies, and Perspectives on Healing).

Subjects: MEDICAL sciences; BLOOD diseases; BETA-Thalassemia

• Source: Gene Therapy Weekly; 12/13/2024, p2240-2240, 1p

Record details

Beta-thalassemia Market to Witness Upsurge in Growth During the Study Period 2019-2032, Evaluates DelveInsight | Leading Companies - Vertex Pharmaceuticals, CRISPR Therapeutics, Agios Pharmaceuticals, Celgene, Forma Therapeutics.

Subjects: BETA-Thalassemia; CRISPRS; DRUGSVERTEX Pharmaceuticals Inc.

• Source: Pharma Business Week; 2/2/2024, p273-273, 1p

Record details

Department of Hematology Researcher Yields New Data on Gene Therapy (Genetic Modifiers of Hemoglobin Expression from a Clinical Perspective in Hemoglobinopathy Patients with Beta Thalassemia and Sickle Cell Disease).

• Source: Gene Therapy Weekly; 11/25/2024, p102-102, 1p

Record details

bluebird bio to Present Additional Long-Term Follow-up Data from Gene Therapy Programs in Sickle Cell Disease and Beta-Thalassemia at the 66th American Society of Hematology (ASH) Annual Meeting and Exposition

• Authors : bluebird bio, Inc.

• Source: Business Wire (English). 11/05/2024.

Record details

Shiraz University of Medical Sciences Researchers Yield New Study Findings on Cancer Gene Therapy (Gene therapy in beta thalassemia: a review article).

Subjects: BETA-Thalassemia; GENE therapy; CANCER genes

• Source: Cancer Gene Therapy Week; 9/25/2023, p330-330, 1p

Record details

An Open-label Clinical Trial of Ex Vivo Beta-globin Lentiviral Vector Transduction of Autologous CD34+HSCs (Vebeglogene Autotemcel) for the Treatment of Beta-thalassemia Patients.

Subjects: CLINICAL trials; BETA-Thalassemia; BLOOD diseases

• Source: Stem Cell Week; 2024, p59-59, 1p

Record details

Vertex Announces CASGEVY™ Reimbursement Agreement for the Treatment of Transfusion-Dependent Beta Thalassemia in England

• Authors : Vertex Pharmaceuticals

• Source: Business Wire (English). 08/07/2024.

Record details

Emory University Researcher Releases New Data on Gene Therapy (Accelerated Atherosclerosis in Beta Thalassemia).

Subjects: BETA-Thalassemia; GENE therapy; ATHEROSCLEROSISEMORY University

• Source: Gene Therapy Weekly; 9/29/2023, p263-263, 1p

Record details

New Gene Therapy Study Results from French National Institute of Health and Medical Research UMR1163 Described [Adenine Base Editor-mediated Correction of the Common and Severe Ivs1-110 (G > A) Beta-thalassemia Mutation].

Subjects: MEDICAL research; GENE therapy; BETA-Thalassemia

• Source: Gene Therapy Weekly; 7/24/2023, p945-945, 1p

Record details

Decision-Making and Quality of Life Surrounding Hematologic Disease and Gene Therapy.

Subjects: SICKLE cell anemia; BLOOD diseases; LYMPHATIC diseases

• Source: Gene Therapy Weekly; 11/11/2024, p780-780, 1p

Record details