Search Results

Gene drives: an alternative approach to malaria control?

• Authors : Naidoo K; SAMRC/Wits Antiviral Gene Therapy Research Unit, Faculty of Health Sciences, University of the Witwatersrand, Johannesburg, South Africa. .; National Health Laboratory Service, Johannesburg, South Africa. .

• Source: Gene therapy [Gene Ther] 2024 Jul 22. Date of Electronic Publication: 2024 Jul 22.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Gene augmentation for autosomal dominant retinitis pigmentosa using rhodopsin genomic loci nanoparticles in the P23H +/- knock-in murine model.

• Authors : Sp S; Department of Ophthalmology, the University of North Carolina at Chapel Hill, Chapel Hill, NC, 27599, USA.; Mitra RN

Subjects: Retinitis Pigmentosa*/Retinitis Pigmentosa*/Retinitis Pigmentosa*/genetics ; Retinitis Pigmentosa*/Retinitis Pigmentosa*/Retinitis Pigmentosa*/therapy ; MicroRNAs*/MicroRNAs*/MicroRNAs*/genetics

• Source: Gene therapy [Gene Ther] 2023 Aug; Vol. 30 (7-8), pp. 628-640. Date of Electronic Publication: 2023 Mar 20.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Identification of RPGR ORF15 mutation for X-linked retinitis pigmentosa in a large Chinese family and in vitro correction with prime editor.

• Authors : Lv X; School of Ophthalmology and Optometry, Eye Hospital, Wenzhou Medical University, State Key Laboratory and Key Laboratory of Vision Science, Ministry of Health and Zhejiang Provincial Key Laboratory of Ophthalmology and Optometry, Wenzhou, Zhejiang, 325027, China.; Zheng Z

Subjects: Eye Proteins*/Eye Proteins*/Eye Proteins*/genetics ; Genetic Diseases, X-Linked*/Genetic Diseases, X-Linked*/Genetic Diseases, X-Linked*/genetics ; Genetic Diseases, X-Linked*/Genetic Diseases, X-Linked*/Genetic Diseases, X-Linked*/therapy

• Source: Gene therapy [Gene Ther] 2023 Feb; Vol. 30 (1-2), pp. 160-166. Date of Electronic Publication: 2022 Jul 06.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Prospects of viral vector-mediated delivery of sequences encoding anti-HBV designer endonucleases.

• Authors : Jacobs R; Wits/SAMRC Antiviral Gene Therapy Research Unit, Faculty of Health Sciences, University of the Witwatersrand, Johannesburg, South Africa.; Singh P

• Source: Gene therapy [Gene Ther] 2022 May 24. Date of Electronic Publication: 2022 May 24.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Genome editing using CRISPR/Cas9 to treat hereditary hematological disorders.

• Authors : Chen Y; Zhanjiang Institute of Clinical Medicine, Zhanjiang Central Hospital, Guangdong Medical University, Zhanjiang, PR China.; Wen R

Subjects: Gene Editing*/Gene Editing*/Gene Editing*/methods ; Hematologic Diseases*/Hematologic Diseases*/Hematologic Diseases*/genetics ; Hematologic Diseases*/Hematologic Diseases*/Hematologic Diseases*/therapy

• Source: Gene therapy [Gene Ther] 2022 May; Vol. 29 (5), pp. 207-216. Date of Electronic Publication: 2021 Mar 09.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Optimization of oncolytic effect of Newcastle disease virus Clone30 by selecting sensitive tumor host and constructing more oncolytic viruses.

• Authors : Liu T; College of Life Science, Northeast Agricultural University, Harbin, 150030, China.; Zhang Y

Subjects: Neoplasms* ; Oncolytic Virotherapy* ; Oncolytic Viruses*/Oncolytic Viruses*/Oncolytic Viruses*/genetics

• Source: Gene therapy [Gene Ther] 2021 Dec; Vol. 28 (12), pp. 697-717. Date of Electronic Publication: 2020 May 14.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Retroviral gene therapy in Germany with a view on previous experience and future perspectives.

• Authors : Morgan, Michael A.; Galla, Melanie; Grez, Manuel

• Source: Gene Therapy. September, 2021, Vol. 28 Issue 9, p494, 19 p.

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Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repair.

• Authors : Sweeney, Colin L.; Pavel-Dinu, Mara; Choi, Uimook

• Source: Gene Therapy. June, 2021, Vol. 28 Issue 6, p373, 18 p.

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Rescue of retinal ganglion cells in optic nerve injury using cell-selective AAV mediated delivery of SIRT1.

• Authors : Ross AG; University of Pennsylvania/Ophthalmology, Philadelphia, PA, USA. .; Center for Advanced Retinal and Ocular Therapeutics, F. M. Kirby Center for Molecular Ophthalmology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. .

Subjects: Optic Nerve Injuries*/Optic Nerve Injuries*/Optic Nerve Injuries*/genetics ; Optic Nerve Injuries*/Optic Nerve Injuries*/Optic Nerve Injuries*/therapy; Animals

• Source: Gene therapy [Gene Ther] 2021 May; Vol. 28 (5), pp. 256-264. Date of Electronic Publication: 2021 Feb 15.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Effect of connective tissue growth factor gene editing using adeno-associated virus-mediated CRISPR-Cas9 on rabbit glaucoma filtering surgery outcomes.

• Authors : Lee, Eun Jung; Han, Jong Chul; Park, Do Young

• Source: Gene Therapy. May, 2021, Vol. 28 Issue 5, p277, 10 p.

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