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Academic Journal

Prophylaxis with recombinant factor IX Fc fusion protein reduces the risk of bleeding and delays time to first spontaneous bleed event in previously untreated patients with haemophilia B: A post hoc analysis of the PUPs B-LONG study.

  • Authors : Nolan B; Haematology Department, Children's Health Ireland at Crumlin, Dublin, Republic of Ireland.; Recht M

Subjects: Factor IX*/Factor IX*/Factor IX*/administration & dosage ; Factor IX*/Factor IX*/Factor IX*/therapeutic use ; Hemophilia B*/Hemophilia B*/Hemophilia B*/drug therapy

  • Source: European journal of haematology [Eur J Haematol] 2024 Oct; Vol. 113 (4), pp. 485-492. Date of Electronic Publication: 2024 Jun 25.Publisher: Blackwell Country of Publication: England NLM ID: 8703985 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1600-0609

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Academic Journal

Transplacental delivery of factor IX Fc-fusion protein ameliorates bleeding phenotype of newborn hemophilia B mice.

  • Authors : Sakurai F; Laboratory of Biochemistry and Molecular Biology, Graduate School of Pharmaceutical Sciences, Osaka University, Osaka, Japan. Electronic address: .; Iizuka S

Subjects: Factor IX*/Factor IX*/Factor IX*/administration & dosage ; Factor IX*/Factor IX*/Factor IX*/genetics ; Hemophilia B*/Hemophilia B*/Hemophilia B*/therapy

  • Source: Journal of controlled release : official journal of the Controlled Release Society [J Control Release] 2024 Oct; Vol. 374, pp. 415-424. Date of Electronic Publication: 2024 Aug 24.Publisher: Elsevier Science Publishers Country of Publication: Netherlands NLM ID: 8607908 Publication Model: Print-Electronic Cited Medium: Internet

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Academic Journal

Characterization of recombinant factor IX fusion proteins enabling subcutaneous administration.

  • Authors : Schön K; Pharmacology & Toxicology, Research, CSL Innovation GmbH, Marburg, Hesse, Germany; Institute of Pharmacology, Biochemical-Pharmacological Center, University of Marburg, Marburg, Hesse, Germany.

Subjects: Factor IX*/Factor IX*/Factor IX*/pharmacokinetics ; Factor IX*/Factor IX*/Factor IX*/genetics ; Factor IX*/Factor IX*/Factor IX*/administration & dosage

  • Source: Journal of thrombosis and haemostasis : JTH [J Thromb Haemost] 2024 Oct; Vol. 22 (10), pp. 2713-2723. Date of Electronic Publication: 2024 Jul 15.Publisher: Elsevier Country of Publication: England NLM ID: 101170508 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1538-7836

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Academic Journal

PBPK modeling of recombinant factor IX Fc fusion protein (rFIXFc) and rFIX to characterize the binding to type 4 collagen in the extravascular space.

Subjects: Collagen Type IV*/Collagen Type IV*/Collagen Type IV*/pharmacokinetics ; Collagen Type IV*/Collagen Type IV*/Collagen Type IV*/metabolism ; Collagen Type IV*/Collagen Type IV*/Collagen Type IV*/administration & dosage

  • Source: CPT: pharmacometrics & systems pharmacology [CPT Pharmacometrics Syst Pharmacol] 2024 Oct; Vol. 13 (10), pp. 1630-1640. Date of Electronic Publication: 2024 Sep 16.Publisher: Wiley Country of Publication: United States NLM ID: 101580011 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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Academic Journal

Blood coagulation factor IX: structural insights impacting hemophilia B therapy.

  • Authors : Bos MHA; Department of Internal Medicine, Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands.; van Diest RE

Subjects: Hemophilia B*/Hemophilia B*/Hemophilia B*/therapy ; Hemophilia B*/Hemophilia B*/Hemophilia B*/genetics ; Hemophilia B*/Hemophilia B*/Hemophilia B*/metabolism

  • Source: Blood [Blood] 2024 Nov 21; Vol. 144 (21), pp. 2198-2210.Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print Cited Medium: Internet ISSN: 1528-0020

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Academic Journal

A novel snake venom C-type lectin-like protein modulates blood coagulation by targeting von Willebrand factor and coagulation factor IX.

  • Authors : Zeng FY; State Key Laboratory of Functions and Applications of Medicinal Plants, Guizhou Medical University, Guiyang, 550014, China.; School of Pharmaceutical Sciences, Guizhou Medical University, Guiyang, 550025, China.

Subjects: von Willebrand Factor*/von Willebrand Factor*/von Willebrand Factor*/metabolism ; Blood Coagulation*/Blood Coagulation*/Blood Coagulation*/drug effects ; Lectins, C-Type*/Lectins, C-Type*/Lectins, C-Type*/metabolism

  • Source: Scientific reports [Sci Rep] 2024 Oct 03; Vol. 14 (1), pp. 22962. Date of Electronic Publication: 2024 Oct 03.Publisher: Nature Publishing Group Country of Publication: England NLM ID: 101563288 Publication Model: Electronic Cited Medium: Internet ISSN:

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Academic Journal

Assessing health care resource use, outcomes, and costs among Medicaid beneficiaries receiving factor IX prophylaxis for hemophilia B.

  • Authors : Pauly N; Manatt Health Strategies, LLC, New York City, NY.; Burrell A

Subjects: Hemophilia B*/Hemophilia B*/Hemophilia B*/drug therapy ; Hemophilia B*/Hemophilia B*/Hemophilia B*/economics ; Medicaid*/Medicaid*/Medicaid*/economics

  • Source: Journal of managed care & specialty pharmacy [J Manag Care Spec Pharm] 2024 Oct; Vol. 30 (10), pp. 1095-1105. Date of Electronic Publication: 2024 Jun 26.Publisher: Academy of Managed Care Pharmacy Country of Publication: United States NLM ID: 101644425 Publication Model: Print-Electronic Cited Medium:

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Academic Journal

Field Study and Correlative Studies of Factor IX Variant FIX-R338L in Participants Treated with Fidanacogene Elaparvovec.

  • Authors : Pittman DD; Rare Disease Research Unit, Pfizer Inc., Cambridge, Massachusetts, United States.; Carrieri C

Subjects: Factor IX*/Factor IX*/Factor IX*/genetics ; Factor IX*/Factor IX*/Factor IX*/metabolism ; Factor IX*/Factor IX*/Factor IX*/therapeutic use

  • Source: Thrombosis and haemostasis [Thromb Haemost] 2024 Oct; Vol. 124 (10), pp. 912-921. Date of Electronic Publication: 2024 Jun 11.Publisher: Thieme Country of Publication: Germany NLM ID: 7608063 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2567-689X

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Academic Journal

An integrated multitool analysis contributes elements to interpreting unclassified factor IX missense variants associated with hemophilia B.

  • Authors : Sacco M; Department of Translational Medicine and Surgery, Catholic University of the Sacred Heart, Rome, Italy.; Testa MF

Subjects: Factor IX*/Factor IX*/Factor IX*/genetics ; Factor IX*/Factor IX*/Factor IX*/metabolism ; Hemophilia B*/Hemophilia B*/Hemophilia B*/genetics

  • Source: Journal of thrombosis and haemostasis : JTH [J Thromb Haemost] 2024 Oct; Vol. 22 (10), pp. 2724-2738. Date of Electronic Publication: 2024 Jul 15.Publisher: Elsevier Country of Publication: England NLM ID: 101170508 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1538-7836

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Academic Journal

Identifying hemophilia B carriers: Utility of aPTT, factor IX levels and ratios of factor IX to other Vitamin K dependent factors.

  • Authors : Shu M; Division of Haematology/Oncology, Department of Paediatrics, The Hospital for Sick Children, Toronto, Ontario, Canada.; Malcolmson C

Subjects: Hemophilia B*/Hemophilia B*/Hemophilia B*/blood ; Hemophilia B*/Hemophilia B*/Hemophilia B*/diagnosis ; Hemophilia B*/Hemophilia B*/Hemophilia B*/genetics

  • Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2024 Jul; Vol. 30 (4), pp. 1003-1009. Date of Electronic Publication: 2024 Jun 24.Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN:

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  • 1-10 of  119,822 results for ""Factor IX""